Research

Mapping the CDC National ALS Registry

September 8, 2023 Comments Off on Mapping the CDC National ALS Registry

At the annual National ALS Registry Research Symposium, hosted by the Centers for Disease Control and Prevention (CDC), there was a special presentation on mapping to better understand the registry’s…

‘New’ ALS gene destabilizes neuron’s structure and nucleus

September 8, 2023 Comments Off on ‘New’ ALS gene destabilizes neuron’s structure and nucleus

The viral ALS Ice Bucket Challenge a few years ago raised major funding that resulted in the discovery of new genes connected to the disease. One of those genes is…

Opportunity to submit comments to FDA about NurOwn

September 8, 2023 Comments Off on Opportunity to submit comments to FDA about NurOwn

On Wednesday, September 27, 2023, the FDA will host a public advisory committee meeting (AdComm) for BrainStorm Cell Therapeutics’ stem cell therapy NurOwn for the treatment of ALS.  The public…

Expanding Diversity in Clinical Trials

June 20, 2023 Comments Off on Expanding Diversity in Clinical Trials

Expanding access to clinical trials is crucial to making ALS livable for everyone, everywhere, until we find a cure. One way to help make that a reality is by making…

Researcher Spotlight: Miriam Linsenmeier, Ph.D., 2022 Milton Safenowitz Postdoctoral Fellow

June 13, 2023 Comments Off on Researcher Spotlight: Miriam Linsenmeier, Ph.D., 2022 Milton Safenowitz Postdoctoral Fellow

To find new treatments and a cure for ALS, it’s vital to have a dedicated network of scientists working to advance our understanding of the disease and thinking creatively about…

Celebrating the Successes of ALS Research Today, While Working to Fund More for the Future

May 9, 2023 Comments Off on Celebrating the Successes of ALS Research Today, While Working to Fund More for the Future

This last year has seen incredible progress in the fight to create a world without ALS. The FDA approval of Relyvrio (AMX0035) in 2022 and Qalsody (tofersen) last month are…

Regenerative Medicine: A New Path for ALS Treatment

May 1, 2023 Comments Off on Regenerative Medicine: A New Path for ALS Treatment

A first-of-its-kind stem cell therapy for ALS passes a critical safety benchmark, advancing the search to slow down, reverse and prevent the disease. In a parallel study, investigators are growing…

FDA approves treatment of ALS associated with a mutation in the SOD1 gene

April 27, 2023 Comments Off on FDA approves treatment of ALS associated with a mutation in the SOD1 gene

On April 25, 2023, the US Food and Drug Administration (FDA) announced that Qalsody (tofersen) HAS BEEN APPROVED as a new prescription therapy for the treatment of people with rare…

FDA Grants Accelerated Approval for QALSODY™ (tofersen) for SOD1-ALS, a Major Scientific Advancement as the First Treatment to Target a Genetic Cause of ALS

April 25, 2023 Comments Off on FDA Grants Accelerated Approval for QALSODY™ (tofersen) for SOD1-ALS, a Major Scientific Advancement as the First Treatment to Target a Genetic Cause of ALS

CAMBRIDGE, Mass., April 25, 2023 (GLOBE NEWSWIRE) — Biogen Inc. (Nasdaq: BIIB) announced today that the U.S. Food and Drug Administration (FDA) has approved QALSODY™ (tofersen) 100 mg/15mL injection for…

The Golden West Chapter Congratulates the 2023 Sheila Essey Award for ALS Research and the Richard Olney MD, Clinician-Scientist Development Award Recipients

April 7, 2023 Comments Off on The Golden West Chapter Congratulates the 2023 Sheila Essey Award for ALS Research and the Richard Olney MD, Clinician-Scientist Development Award Recipients

Since 1996, the Sheila Essey Award for ALS Research  has been presented to acknowledge and honor an individual who is making significant contributions and breakthroughs in the search for the…